ATX100 is a biodegradable ionizable lipid with improved in vivo activities for siRNA delivery via lipid nanoparticles (LNP). The physicochemical parameters of ATX100: pKa 6.316, lipophilicity cLogD 14.03, nanoparticle size 82 nm. The in vivo factor VII knockdown efficiency of ATX100 is 97% (0.03mg/kg in mice, i.v.).
Categories | Lipids |
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Filter | Ionizable/Cationic Lipids |
CAS Number | 2230647-37-5 |
Molecular Formula | C44H86N2O5S |
Molecular Weight (g/mol) | 755.24 |
Purity | >95% |
Storage | -20 °C or below |